Two of Opus's seven gene therapy assets are in clinical trials, with additional programs expected to enter the clinic.

Mutations in the tumor suppressor TP53 are a common cause of cancer, making the altered protein an attractive target for ...

Genetic variants believed to cause blindness in nearly everyone who carries them actually lead to vision loss less than 30% ...

DNA doesn’t just sit still inside our cells — it folds, loops, and rearranges in ways that shape how genes behave.

Orphan Drug Designation applies to approximately 50,000 Patients who predominantly suffer from severe chronic pain due to ...

This penguin’s features are very special and rare. @bbcearth explains, "This Gentoo penguin's stark white [color] is the ...

Deafness, the most common sensorineural hearing loss at all stages of life, occurs either independently or as part of ...

Gene that drops early in pancreatic tumors linked to shorter survival at stage II. Findings could guide future treatment ...

A new single-cell profiling technique has mapped pre-malignant gene mutations and their effects in solid tissues for the first time, in a study led by investigators at Weill Cornell Medicine and the ...

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited ...

Deep in the rolling countryside of Breckerfeld, Germany, lives the tiny superstar featured in this YouTube video — an ...

In a new study, terrestrial bacteria-infecting viruses were still able to infect their E. coli hosts in near-weightless ...